A model-informed clinical trial simulation tool with a graphical user interface for Duchenne muscular dystrophy

Jongjin Kim, Juan Francisco Morales, Sanghoon Kang, Marian Klose, Rebecca J. Willcocks, Michael J. Daniels, Ramona Belfiore-Oshan, Glenn A. Walter, William D. Rooney, Krista Vandenborne, Sarah Kim

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Pharmacology, Toxicology and Pharmaceutical Science

Biochemistry, Genetics and Molecular Biology

Computer Science

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