Cognitive endpoints for therapy development for neuronopathic mucopolysaccharidoses: Results of a consensus procedure

Johanna H. van der Lee, Jonathan Morton, Heather R. Adams, Lorne Clarke, Berendine Johanne Ebbink, Maria L. Escolar, Roberto Giugliani, Paul Harmatz, Melissa Hogan, Simon Jones, Shauna Kearney, Joseph Muenzer, Stewart Rust, Margaret Semrud-Clikeman, Frits A. Wijburg, Zi fan Yu, Darren Janzen, Elsa Shapiro