Pantothenate kinase-associated neurodegeneration (Pkan)

Research output: Chapter in Book/Report/Conference proceedingChapter


Significant gains in our understanding of the biochemical defects in PKAN have shifted the therapeutic focus from palliative care to rational interventions. Novel therapies aimed at correcting specific perturbations in cellular metabolism hold great promise and are currently under investigation. Treatment of this rare neurode-generative disorder is likely to change significantly over the next decade.

Original languageEnglish (US)
Title of host publicationTreatment of Pediatric Neurologic Disorders
PublisherCRC Press
Number of pages5
ISBN (Electronic)9780849340888
ISBN (Print)0824726936, 9780824726935
StatePublished - Jan 1 2005

ASJC Scopus subject areas

  • Medicine(all)


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