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Stargardt Disease: Gene Therapy Strategies for ABCA4

Research output: Contribution to journalArticlepeer-review

Original languageEnglish (US)
Pages (from-to)157-165
Number of pages9
JournalInternational ophthalmology clinics
Volume61
Issue number4
DOIs
StatePublished - 2021

Funding

Supported by Sanofi, AGTC, Biogen, 4D, ProQR, FFB, Editas/Allergan, Acucela for clinical trial.

Funders
Biogen
Applied Genetic Technologies Corporation

    ASJC Scopus subject areas

    • Ophthalmology

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