Cross-sectional validation study of patient-reported outcomes in patients with paroxysmal nocturnal haemoglobinuria

I. Weitz, G. Meyers, T. Lamy, J. Y. Cahn, M. T. Uranga, J. A. García Vela, M. A. Sanz, B. Severino, R. J. Kelly, P. Hillmen, A. Hill

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