Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study
Thomas Klopstock, Fernando Tricta, Lynne Neumayr, Ivan Karin, Giovanna Zorzi, Caroline Fradette, Tomasz Kmieć, Boriana Büchner, Hannah E. Steele, Rita Horvath, Patrick F. Chinnery, Anna Basu, Clemens Küpper, Christiane Neuhofer, Bernadette Kálmán, Petr Dušek, Zuhal Yapici, Ian Wilson, Feng Zhao, Federica ZibordiNardo Nardocci, Christine Aguilar, Susan J. Hayflick, Michael Spino, Andrew M. Blamire, Penelope Hogarth, Elliott Vichinsky
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