Strategies for Treating Inherited Retinal Degeneration with Large Genes That Are Not Amenable to Adeno-Associated Virus-Based Gene Replacement Therapy

Paul Yang, Mark E. Pennesi, Richard G. Weleber

Research output: Contribution to journalComment/debatepeer-review

Original languageEnglish (US)
Pages (from-to)328-329
Number of pages2
JournalJAMA ophthalmology
Volume139
Issue number3
DOIs
StatePublished - Mar 2021

ASJC Scopus subject areas

  • Ophthalmology

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